Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Human Alpha-L-Iduronidase in Rhesus Macaques
Open Access
- 1 September 2018
- journal article
- research article
- Published by Elsevier BV in Molecular Therapy - Methods & Clinical Development
- Vol. 10, 79-88
- https://doi.org/10.1016/j.omtm.2018.06.003
Abstract
No abstract availableFunding Information
- University of Pennsylvania
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