Personalized exon skipping strategies to address clustered non-deletion dystrophin mutations
- 31 December 2010
- journal article
- Published by Elsevier BV in Neuromuscular Disorders
- Vol. 20 (12), 810-816
- https://doi.org/10.1016/j.nmd.2010.07.276
Abstract
No abstract availableFunding Information
- the National Institutes of Health (2 R01 NS044146-05A1)
- the Muscular Dystrophy Association, USA (4352)
- Suneels’s Light
- Charley’s Fund
- the Killowen Fundraising Group
- Gavriel Meir Trust
- the Muscular Dystrophy Association WA Inc.
- the Medical and Health Research Infrastructure Fund of Western Australia
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