Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy
Open Access
- 5 July 2007
- journal article
- Published by Springer Science and Business Media LLC in BMC Medical Genetics
- Vol. 8 (1), 43
- https://doi.org/10.1186/1471-2350-8-43
Abstract
No abstract availableKeywords
This publication has 18 references indexed in Scilit:
- Exploring the Frontiers of Therapeutic Exon Skipping for Duchenne Muscular Dystrophy by Double Targeting within One or Multiple ExonsMolecular Therapy, 2006
- Duplications in theDMD geneHuman Mutation, 2006
- Entries in the Leiden Duchenne muscular dystrophy mutation database: An overview of mutation types and paradoxical cases that confirm the reading‐frame ruleMuscle & Nerve, 2006
- Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathologyNature Medicine, 2006
- Functional Analysis of 114 Exon-Internal AONs for Targeted DMD Exon Skipping: Indication for Steric Hindrance of SR Protein Binding SitesOligonucleotides, 2005
- Antisense-Induced Multiexon Skipping for Duchenne Muscular Dystrophy Makes More SenseAmerican Journal of Human Genetics, 2004
- Exploiting the Natural Diversity in Adenovirus Tropism for Therapy and Prevention of DiseaseJournal of Virology, 2002
- The muscular dystrophiesThe Lancet, 2002
- Application of in vitro myo-differentiation of non-muscle cells to enhance gene expression and facilitate analysis of muscle proteinsNeuromuscular Disorders, 1996
- Characterization of Dystrophin in Muscle-Biopsy Specimens from Patients with Duchenne's or Becker's Muscular DystrophyThe New England Journal of Medicine, 1988