Outcomes of transplantation using various hematopoietic cell sources in children with Hurler syndrome after myeloablative conditioning
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Open Access
- 9 May 2013
- journal article
- Published by American Society of Hematology in Blood
- Vol. 121 (19), 3981-3987
- https://doi.org/10.1182/blood-2012-09-455238
Abstract
Key Points In HS, patients’ early referral for HCT, with the best available HLA-matched donor offers the best event-free survival. In HS, patients’ HCT with a well-matched unrelated cord blood unit is particularly attractive because the unit is readily available.Keywords
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