A decade of optimizing drug development for rare neuromuscular disorders through TACT
- 1 January 2020
- journal article
- editorial
- Published by Springer Science and Business Media LLC in Nature Reviews Drug Discovery
- Vol. 19 (1), 1-2
- https://doi.org/10.1038/d41573-019-00199-1
Abstract
No abstract availableThis publication has 2 references indexed in Scilit:
- The TREAT-NMD advisory committee for therapeutics (TACT): an innovative de-risking model to foster orphan drug developmentOrphanet Journal of Rare Diseases, 2015
- Enhancing translation: Guidelines for standard pre-clinical experiments in mdx miceNeuromuscular Disorders, 2012