B-cell depletion is protective against anti-AAV capsid immune response: a human subject case study
Open Access
- 1 January 2014
- journal article
- Published by Elsevier BV in Molecular Therapy - Methods & Clinical Development
- Vol. 1, 14033
- https://doi.org/10.1038/mtm.2014.33
Abstract
No abstract availableThis publication has 50 references indexed in Scilit:
- Prevalence and pharmacological modulation of humoral immunity to AAV vectors in gene transfer to synovial tissueGene Therapy, 2012
- Mapping the T helper cell response to acid α-glucosidase in Pompe miceMolecular Genetics and Metabolism, 2012
- Gene Therapy for Leber Congenital Amaurosis Caused by RPE65 MutationsJAMA Ophthalmology, 2012
- Capsid-specific T-cell Responses to Natural Infections With Adeno-associated Viruses in Humans Differ From Those of Nonhuman PrimatesMolecular Therapy, 2011
- Dystrophin Immunity in Duchenne's Muscular DystrophyThe New England Journal of Medicine, 2010
- Rituximab: Mechanism of ActionSeminars in Hematology, 2010
- Progress and prospects: immune responses to viral vectorsGene Therapy, 2009
- Sustained transgene expression despite T lymphocyte responses in a clinical trial of rAAV1-AAT gene therapyProceedings of the National Academy of Sciences of the United States of America, 2009
- Vision 1 Year after Gene Therapy for Leber's Congenital AmaurosisThe New England Journal of Medicine, 2009
- Neural deficits contribute to respiratory insufficiency in Pompe diseaseProceedings of the National Academy of Sciences of the United States of America, 2009