Dose-dependent responses to macrophage-targeted glucocerebrosidase in a child with Gaucher disease
- 29 February 1992
- journal article
- case report
- Published by Elsevier BV in The Journal of Pediatrics
- Vol. 120 (2), 277-280
- https://doi.org/10.1016/s0022-3476(05)80444-5
Abstract
No abstract availableKeywords
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- Therapeutic response to intravenous infusions of glucocerebrosidase in a patient with Gaucher disease.Proceedings of the National Academy of Sciences of the United States of America, 1990
- Replacement Therapy for Inherited Enzyme DeficiencyNew England Journal of Medicine, 1974
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