Agreement between the results of meta-analyses from case reports and from clinical studies regarding the efficacy of laronidase therapy in patients with mucopolysaccharidosis type I who initiated enzyme replacement therapy in adult age: An example of case reports meta-analyses as an useful tool for evidence-based medicine in rare diseases
- 1 February 2018
- journal article
- review article
- Published by Elsevier BV in Molecular Genetics and Metabolism
- Vol. 123 (2), 69-75
- https://doi.org/10.1016/j.ymgme.2018.01.002
Abstract
No abstract availableKeywords
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