Rate of progression and predictive factors for pulmonary outcome in children and adults with Pompe disease
- 31 October 2011
- journal article
- research article
- Published by Elsevier BV in Molecular Genetics and Metabolism
- Vol. 104 (1-2), 129-136
- https://doi.org/10.1016/j.ymgme.2011.06.012
Abstract
No abstract availableKeywords
Funding Information
- Erasmus MC Revolving Fund
- European Union, 7th Framework Programme “Euclyd — a European Consortium for Lysosomal Storage Diseases” (201678)
- ZonMw (152001005)
- Prinses Beatrix Fonds (OP07-08)
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