The diagnostic journey of patients with mucopolysaccharidosis I: A real-world survey of patient and physician experiences
Open Access
- 1 September 2016
- journal article
- Published by Elsevier BV in Molecular Genetics and Metabolism Reports
- Vol. 8, 67-73
- https://doi.org/10.1016/j.ymgmr.2016.07.006
Abstract
No abstract availableKeywords
Funding Information
- Sanofi
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