Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease
Open Access
- 5 January 2012
- journal article
- research article
- Published by Elsevier BV in Genetics in Medicine
- Vol. 14 (1), 135-142
- https://doi.org/10.1038/gim.2011.4
Abstract
No abstract availableKeywords
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