The attenuated/late onset lysosomal storage disorders: Therapeutic goals and indications for enzyme replacement treatment in Gaucher and Fabry disease
- 1 March 2015
- journal article
- review article
- Published by Elsevier BV in Best Practice & Research Clinical Endocrinology & Metabolism
- Vol. 29 (2), 205-218
- https://doi.org/10.1016/j.beem.2014.08.006
Abstract
No abstract availableKeywords
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