Sustained and Complete Phenotype Correction of Hemophilia B Mice Following Intramuscular Injection of AAV1 Serotype Vectors
Open Access
- 30 September 2001
- journal article
- Published by Elsevier BV in Molecular Therapy
- Vol. 4 (3), 217-222
- https://doi.org/10.1006/mthe.2001.0449
Abstract
No abstract availableKeywords
This publication has 27 references indexed in Scilit:
- Factors influencing in vivo transduction by recombinant adeno-associated viral vectors expressing the human factor IX cDNABlood, 2001
- Several Log Increase in Therapeutic Transgene Delivery by Distinct Adeno-Associated Viral Serotype VectorsMolecular Therapy, 2000
- Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vectorNature Genetics, 2000
- The Use of Adeno-Associated Virus to Circumvent the Maturation-Dependent Viral Transduction of Muscle FibersHuman Gene Therapy, 2000
- Persistent expression of canine factor IX in hemophilia B caninesGene Therapy, 1999
- Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vectorNature Medicine, 1999
- Human Factor IX Corrects the Bleeding Diathesis of Mice With Hemophilia BBlood, 1998
- Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virusProceedings of the National Academy of Sciences of the United States of America, 1997
- Haemophilia prophylaxis in young patients–a long‐term follow‐upJournal of Internal Medicine, 1997
- Adeno-associated Viral VectorsPublished by Springer Science and Business Media LLC ,1995