Lessons Learned From Vivo-Morpholinos: How to Avoid Vivo-Morpholino Toxicity

Abstract
Vivo-morpholinos are a promising tool for gene silencing. These oligonucleotide analogs transiently silence genes by blocking either translation or pre-mRNA splicing. Little to no toxicity has been...
Funding Information
  • Department of Health and Kinesiology (AR050085)