Functional rescue of c.3846G>A (W1282X) in patient-derived nasal cultures achieved by inhibition of nonsense mediated decay and protein modulators with complementary mechanisms of action
Open Access
- 9 December 2019
- journal article
- research article
- Published by Elsevier BV in Journal of Cystic Fibrosis
- Vol. 19 (5), 717-727
- https://doi.org/10.1016/j.jcf.2019.12.001
Abstract
No abstract availableKeywords
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