Efficacy of Gene Therapy for a Prototypical Lysosomal Storage Disease (GSD-II) Is Critically Dependent on Vector Dose, Transgene Promoter, and the Tissues Targeted for Vector Transduction
Open Access
- 30 April 2002
- journal article
- Published by Elsevier BV in Molecular Therapy
- Vol. 5 (4), 436-446
- https://doi.org/10.1006/mthe.2002.0563
Abstract
No abstract availableKeywords
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