Current Translational Research and Murine Models For Duchenne Muscular Dystrophy
Open Access
- 3 March 2016
- journal article
- review article
- Published by IOS Press in Journal of Neuromuscular Diseases
- Vol. 3 (1), 29-48
- https://doi.org/10.3233/jnd-150113
Abstract
Duchenne muscular dystrophy (DMD) is an X-linked genetic disorder characterized by progressive muscle degeneration. Mutations in the DMD gene result in the absence of dystrophin, a protein required for muscle strength and stability. Currently, thereThis publication has 167 references indexed in Scilit:
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