Regression of symptoms after selective iron chelation therapy in a case of neurodegeneration with brain iron accumulation
- 24 April 2008
- journal article
- case report
- Published by Wiley in Movement Disorders
- Vol. 23 (6), 904-907
- https://doi.org/10.1002/mds.22002
Abstract
We report the results of iron chelating treatment with deferiprone in a 61‐year‐old woman with signs and symptoms of neurodegeneration with brain iron accumulation (NBIA). After 6 months of therapy the patient's gait had improved and a reduction in the incidence of choreic dyskinesias was observed. Her gait returned to normal after an additional 2 months of therapy, at which time there was a further reduction in involuntary movements and a partial resolution of the blepharospasm. © 2008 Movement Disorder SocietyKeywords
Funding Information
- Thelethon (Project number GGP05141)
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