Fabry Disease: Preclinical Studies Demonstrate the Effectiveness of α-Galactosidase A Replacement in Enzyme-Deficient Mice
- 1 January 2001
- journal article
- Published by Elsevier BV in American Journal of Human Genetics
- Vol. 68 (1), 14-25
- https://doi.org/10.1086/316953
Abstract
No abstract availableKeywords
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