Safe, Efficient, and Reproducible Gene Therapy of the Brain in the Dog Models of Sanfilippo and Hurler Syndromes
Open Access
- 1 February 2011
- journal article
- research article
- Published by Elsevier BV in Molecular Therapy
- Vol. 19 (2), 251-259
- https://doi.org/10.1038/mt.2010.265
Abstract
No abstract availableKeywords
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