Replacing acid α-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from type II muscle fibers
Open Access
- 1 January 2005
- journal article
- research article
- Published by Elsevier BV in Molecular Therapy
- Vol. 11 (1), 48-56
- https://doi.org/10.1016/j.ymthe.2004.09.017
Abstract
No abstract availableKeywords
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