iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation
Open Access
- 1 June 2020
- journal article
- research article
- Published by Elsevier BV in Molecular Therapy - Methods & Clinical Development
- Vol. 17, 858-870
- https://doi.org/10.1016/j.omtm.2020.04.005
Abstract
No abstract availableFunding Information
- Spanish Ministry for Science and Innovation (PLE2009-0091, RTC-2014-2207-1, IPT-2011-1402-900000, ISCIII PI14/01073)
- ERDF/ESF
- Balearic Government (16023/2008)
- Spanish Cystic Fibrosis Federation
- Federación ASEM-Telemaratón
- Fundación Salud 2000
- European Commission (H2020, PHC-667079)
- METROVACESA
- Basque Government (JCI-2006-2675, PTQ-16-08496)
- Spanish Ministry for Science and Innovation
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