βT87Q-Globin Gene Therapy Reduces Sickle Hemoglobin Production, Allowing for Ex Vivo Anti-sickling Activity in Human Erythroid Cells
Open Access
- 12 June 2020
- journal article
- research article
- Published by Elsevier BV in Molecular Therapy - Methods & Clinical Development
- Vol. 17, 912-921
- https://doi.org/10.1016/j.omtm.2020.04.013
Abstract
No abstract availableThis publication has 45 references indexed in Scilit:
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