CRISPR/dCas9-based Scn1a gene activation in inhibitory neurons ameliorates epileptic and behavioral phenotypes of Dravet syndrome model mice
Open Access
- 21 May 2020
- journal article
- research article
- Published by Elsevier BV in Neurobiology of Disease
- Vol. 141, 104954
- https://doi.org/10.1016/j.nbd.2020.104954
Abstract
No abstract availableKeywords
Funding Information
- RIKEN Center for Brain Science
- RIKEN-CBS
- Takeda Pharmaceutical Company Ltd.
- AMED (JP18dm0107092)
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