Modelling Charcot-Marie-Tooth disease in a dish reveals common cell type-specific alterations
Open Access
- 4 August 2021
- journal article
- editorial
- Published by Oxford University Press (OUP) in Brain
- Vol. 144 (8), 2234-2236
- https://doi.org/10.1093/brain/awab278
Abstract
This scientific commentary refers to ‘Induced pluripotent stem cell-derived motor neurons of CMT type 2 patients reveal progressive mitochondrial dysfunction’, by Van Lent et al. (doi:10.1093/brain/awab226).Funding Information
- Wellcome Trust (109915/Z/15/Z)
- Medical Research Council (MR/N025431/1, MR/V009346/1)
- European Research Council (309548)
- Addenbrookes Charitable Trust (G100142)
- Evelyn Trust, the Stoneygate Trust
- Lily Foundation
- International Centre for Genomic Medicine in Neuromuscular Diseases (MR/S005021/1)
- NIHR
- Cambridge Biomedical Research Centre (BRC-1215-20014)
- NIHR
- Department of Health and Social Care
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