Targeting G542X CFTR nonsense alleles with ELX-02 restores CFTR function in human-derived intestinal organoids
Open Access
- 5 February 2021
- journal article
- research article
- Published by Elsevier BV in Journal of Cystic Fibrosis
- Vol. 20 (3), 436-442
- https://doi.org/10.1016/j.jcf.2021.01.009
Abstract
No abstract availableKeywords
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