Natural Exon Skipping Sets the Stage for Exon Skipping as Therapy for Dystrophic Epidermolysis Bullosa
Open Access
- 19 September 2019
- journal article
- research article
- Published by Elsevier BV in Molecular Therapy Nucleic Acids
- Vol. 18, 465-475
- https://doi.org/10.1016/j.omtn.2019.09.009
Abstract
No abstract availableFunding Information
- Netherlands Organisation for Health Research and Development
- Clinical Fellowship (90715614)
- Priority Medicines Rare Disease
- Dutch Butterfly Child Foundation
- COST Action BM1207
- COST Action CA17103
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